Biostatistical Challenges of Trials in Rare Diseases
April 26, 2018
IDDI Free Live Webinar on Biostatistical Challenges of Trials in Rare Diseases
In this webinar:
- We will start by briefly reviewing the European and international initiatives on rare diseases.
- We will describe special statistical designs and analysis methodologies to address the problem of small populations. Innovative methodologies in the design and analysis of clinical trials in small population groups will be summarized focusing on results from the IDeAl project (IntegratedDEsign and AnaLysis of clinical trials in small population groups).
- Ongoing efforts to bring the innovative methodology into practice and the next steps will be addressed in the conclusion.